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Biotech

Regenxbio starts pivotal study for DMD gene therapy

Regenxbio’s gene therapy improved muscle function for patients with DMD in a phase 1/2 study, with the biotech rolling the trial into a pivotal study.
Gabrielle Masson Nov 18, 2024 2:24pm
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Sarepta's next DMD drug seems to get the job done in phase 2

Jan 29, 2024 10:49am