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Niemann-Pick type C disease

MA strategy deal block push come together form
Biotech

Cyclo Therapeutics merges with longtime backer Rafael Holdings

Cyclo’s lead asset is Trappsol Cyclo, a formulation of hydroxypropyl beta cyclodextrin being evaluated in Niemann-Pick disease type C1.
James Waldron Aug 22, 2024 8:50am
accelerated

'Clinical intuition' led FDA advisors to back Zevra's rare disease med

Aug 5, 2024 10:35am
signing contract

Orphazyme meme ends with $13M sale to satisfy bankruptcy court

May 16, 2022 6:06am
Amsterdam canal

Roche-partnered Scenic nabs $31M to test 3 rare disease meds

Mar 10, 2022 10:12am
Lots of nos

Orphazyme to assess strategic options after EU advisers nix drug

Feb 24, 2022 10:45am
money

Pfizer, NEA-backed rare disease startup bumps up Series A to $42M

Jul 25, 2016 10:32am

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